Gene Therapy for SCID: Q&A with Dr. Sung-Yun Pai
Dr. Sung-Yun Pai is co-director of the Gene Therapy Program, senior physician, and associate professor of pediatrics at the Harvard Medical School. Her laboratory focuses on the study of disorders of human T and B cell development and function, and treatment of these disorders by allogeneic hematopoietic cell transplantation and gene therapy.
Read MoreNew Jersey Governor Signs Legislation Helping to Address High Out-of-Pocket Costs
The Immune Deficiency Foundation (IDF) is happy to announce that yesterday, New Jersey Governor Phil Murphy signed legislation to help the state’s families by making it easier for individuals who depend on expensive prescription drugs to afford their healthcare. IDF is proud to have been a member of a coalition of organizations representing
Read MoreCall to Action - Save the Nation’s Newborn Screening Advisory Committee
Every year, more than 12,000 infants are born with health conditions, such as severe combined immunodeficiency (SCID), that are not apparent at birth, but can cause serious health problems or even death if not treated early. And every year, these babies receive timely life-saving or life-altering care because of newborn screening. Newborn
Read MoreUrgent: Biologic Withdrawal Information for Gamunex (Two Lots)
December 31, 2019 Grifols Therapeutics LLC has initiated a voluntary withdrawal of Gamunex. Click here to read the notification from the Patient Notification System. December 17, 2019 Grifols Therapeutics LLC has initiated a voluntary withdrawal of Gamunex. Click here to read the notification from the Patient Notification System.
Read MoreGrifols launches XEMBIFY®
XEMBIFY®, Grifols’ first 20% subcutaneous immunoglobulin for Primary Immunodeficiency (PI) treatment, is now available in the U.S. Read the press release here.
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